Sarepta has stopped developing SRP-5051, its exon 51-skipping therapy for Duchenne MD, due to long-term safety concerns and ...
Specific mutations in the DMD gene influence how long patients retain the ability to walk, even when treated with ...
Columnist Betty Vertin wishes she could take away the pain over the milestones in the teenage years her sons with DMD will miss.
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback